1999 (v1)
Publication
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Uploaded on: April 14, 2023
C
Last name: COSSU G
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Deferiprone was shown to reverse iron deposition in Friedreich's ataxia. This multi-center, unblinded, single-arm pilot study evaluated safety and efficacy of deferiprone for reducing cerebral iron accumulation in neurodegeneration with brain iron accumulation. Four patients with genetically- confirmed pantothenate kinase-associated...