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MUNI‐LOFRA , Robert

Last name: MUNI‐LOFRA

First name: Robert

2024 (v1)

Publication

Metadata-only

Determining minimal clinically important differences in the Hammersmith Functional Motor Scale Expanded for untreated spinal muscular atrophy patients: An international study

Coratti, Giorgia Bovis, Francesca Pera, Maria Carmela

Background and purposeSpinal muscular atrophy (SMA) is a rare and progressive neuromuscular disorder with varying severity levels. The aim of the study was to calculate minimal clinically important difference (MCID), minimal detectable change (MDC), and values for the Hammersmith Functional Motor Scale Expanded (HFMSE) in an untreated...

Uploaded on: October 21, 2024