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ZOLKIPLI-CUNNINGHAM Z.

Last name: ZOLKIPLI-CUNNINGHAM Z.

2023 (v1)

Publication

Metadata-only

2-Year Change in Revised Hammersmith Scale Scores in a Large Cohort of Untreated Paediatric Type 2 and 3 SMA Participants

Stimpson G. Ramsey D. Wolfe A.

The Revised Hammersmith Scale (RHS) is a 36-item ordinal scale developed using clinical expertise and sound psychometrics to investigate motor function in participants with Spinal Muscular Atrophy (SMA). In this study, we investigate median change in the RHS score up to two years in paediatric SMA 2 and 3 participants and contextualise it to...

Uploaded on: February 14, 2024